参考文献:
PTC THERAPEUTICS, INC. F. HOFFMANN-LA ROCHE AG WOLL, Matthew G. CHEN, Guangming CHOI, Soongyu DAKKA, Amal HUANG, Song KARP, Gary Mitchell LEE, Chang-Sun LI, Chunshi NARASIMHAN, Jana NARYSHKIN, Nikolai PAUSHKIN, Sergey QI, Hongyan TURPOFF, Anthony A. WEETALL, Marla L. WELCH, Ellen YANG, Tianle ZHANG, Nanjing ZHANG, Xiaoyan ZHAO, Xin PINARD, Emmanuel RATNI, Hasane Patent: WO13/11974 A1, 13 Location in patent: Paragraph 586 588